Ongoing research on achondroplasia

There is currently no cure or pharmacological treatment available for achondroplasia. Current care for achondroplasia manages the symptoms

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FDA committees conclusions on the open meeting on achondroplasia

On the 11th May 2018, the FDA (US Food & Drug Administration) held an open session with the Pediatric Advisory Committee (PAC)

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Clinical trial with Meclozine for achondroplasia

Professor Hiroshi Kitoh and his research team from the Graduate School of Medicine

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ALPE summer camp: See you in a year!

This was a camp, like everything else, intense and full of great and small adventures ...

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Therachon starts a Natural History Study in children with achondroplasia

"Dreambird" is the name of the natural history study that Therachon announced on the 21st June 2018.

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BioMarin starts the phase 2 study BMN 111-206 in infants and toddlers

On the 18th June 2018, it was made public that the first patient under 5 years-old was dosed with Vosoritide.

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New potential treatment in development for achondroplasia

QED Therapeutics is a biotechnology company focused on precision medicine for FGFR-driven disorders.

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4th ALPE Awards

The 4th edition of the ALPE Awards have the following winners:

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ALPE participates at the annual convention of the French association APPT

On May 19, 20 and 21, ALPE coordinators

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